Papers: 10.1371/journal.pmed.1003222

https://doi.org/10.1371/journal.pmed.1003222

Efficacy and safety of vamorolone in Duchenne muscular dystrophy: An 18-month interim analysis of a non-randomized open-label extension study

Cited by: 36
Author(s): Edward C. Smith, Laurie S. Conklin, Eric P. Hoffman, Paula R. Clemens, Jean K. Mah, Richard S. Finkel, Michela Guglieri, M. Tulinius, Yoram Nevo, Monique M. Ryan, Richard Webster, Diana Castro, Nancy L. Kuntz, Laurie J. Kerchner, Lauren P. Morgenroth, Adrienne Arrieta, Maya Shimony, Mark Jaros, Phil Shale, Heather Gordish‐Dressman, Laura Hagerty, Utkarsh J. Dang, Jesse M. Damsker, Benjamin D. Schwartz, L. Mengle-Gaw, Craig McDonald, Dnhs Investigators
Published: almost 6 years ago

Software Mentions 1

pypi: PACE
Data Quality of Experimental Data
Papers that mentioned: 13,779
Very Likely Science (90)