Papers: 10.1371/journal.pmed.1003222
https://doi.org/10.1371/journal.pmed.1003222
Efficacy and safety of vamorolone in Duchenne muscular dystrophy: An 18-month interim analysis of a non-randomized open-label extension study
Cited by: 36
Author(s): Edward C. Smith, Laurie S. Conklin, Eric P. Hoffman, Paula R. Clemens, Jean K. Mah, Richard S. Finkel, Michela Guglieri, M. Tulinius, Yoram Nevo, Monique M. Ryan, Richard Webster, Diana Castro, Nancy L. Kuntz, Laurie J. Kerchner, Lauren P. Morgenroth, Adrienne Arrieta, Maya Shimony, Mark Jaros, Phil Shale, Heather Gordish‐Dressman, Laura Hagerty, Utkarsh J. Dang, Jesse M. Damsker, Benjamin D. Schwartz, L. Mengle-Gaw, Craig McDonald, Dnhs Investigators
Published: almost 6 years ago
Software Mentions 1
Very Likely Science (90)